Cas9/gRNA targeted excision of cystic fibrosis-causing deep-intronic splicing mutations restores normal splicing of CFTR mRNA
- Sanz, D.J.
- Hollywood, J.A.
- Scallan, M.F.
- Harrison, P.T.
Revista:
PLoS ONE
ISSN: 1932-6203
Any de publicació: 2017
Volum: 12
Número: 9
Tipus: Article