Cas9/gRNA targeted excision of cystic fibrosis-causing deep-intronic splicing mutations restores normal splicing of CFTR mRNA

  1. Sanz, D.J.
  2. Hollywood, J.A.
  3. Scallan, M.F.
  4. Harrison, P.T.
Journal:
PLoS ONE

ISSN: 1932-6203

Year of publication: 2017

Volume: 12

Issue: 9

Type: Article

DOI: 10.1371/JOURNAL.PONE.0184009 GOOGLE SCHOLAR lock_openOpen access editor